A Potential Autism Cure: New Research Reveals Gene Therapy Could Treat Pitt-Hopkins Syndrome
A new study has shown that gene therapy could prevent or reverse many deleterious effects of Pitt-Hopkins syndrome New research from the UNC Neuroscience Center lab of Ben Philpot, Ph.D., reveals that restoring lost gene activity prevents many signs of disease in an animal model of Pitt-Hopkins syndrome, a rare monogenic neurodevelopmental disorder . Pitt-Hopkins …
