therapy

DNA Gene Therapy Concept

A Potential Autism Cure: New Research Reveals Gene Therapy Could Treat Pitt-Hopkins Syndrome

A new study has shown that gene therapy could prevent or reverse many deleterious effects of Pitt-Hopkins syndrome New research from the UNC Neuroscience Center lab of Ben Philpot, Ph.D., reveals that restoring lost gene activity prevents many signs of disease in an animal model of Pitt-Hopkins syndrome, a rare monogenic neurodevelopmental disorder . Pitt-Hopkins …

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Experimental gene therapy appears to have helped a patient with advanced pancreatic cancer

An experimental treatment appears to have succeeded in halting the progression of a woman’s advanced pancreatic cancer, doctors in the New England Journal of Medicine. The apparent success of the therapy – which involves modifying the genes of immune cells so that they attack tumor cells – could be a major advance in the treatment …

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